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1 Assessment of rAAV2/2-ND4 Gene Therapy Efficacy in LHON Using an External Control GroupNancy J. Newman; Patrick Yu-Wai-Man; Valerio Carelli; Mark Moster; Catherine Vignal-Clermont; Alfredo Sadun; Chiara La Morgia; Francesco Bandello; Lorena Castillo Campillo; Stéphanie Leruez; Dean Cestari; Rod Foroozan; Rustum Karanija; Laure Blouin; Michel Roux; Magali Taiel; José-Alain SahelNANOS Annual Meeting 2021: Scientific Platform Session II
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