| Identifier |
20220215_nanos_sciplatform3_06 |
| Title |
REFLECT Trial: Efficacy and Safety of Bilateral Gene Therapy for Leber Hereditary Optic Neuropathy |
| Creator |
Nancy Newman, Patrick Yu-Wai-Man, Valerio Carelli, Prem Subramanyan4, Mark Moster, An-Guor Wang, Sean Donahue, Bart Leroy, Valérie Biousse, Catherine Vignal-Clermont, Alfredo Sadun, Gema Rebolleda Fernández, Elizabeth Fortin, Rudrani Banik, Laure Blouin, Michel Roux, Magali Taiel, José-Alain Sahe |
| Subject |
Genetic Disease; Optic Neuropathy; Retina |
| Description |
Leber Hereditary Optic Neuropathy (LHON) is a blinding orphan disease leading to bilateral vision loss. Lenadogene nolparvovec (rAAV2/2-ND4) is a gene therapy developed for the treatment of LHON caused by a mutation in the ND4 gene. |
| Date |
2022-02 |
| Language |
eng |
| Format |
application/pdf |
| Type |
Text |
| Source |
2022 North American Neuro-Ophthalmology Society Annual Meeting |
| Relation is Part of |
NANOS Annual Meeting 2022: Scientific Platform III |
| Collection |
Neuro-ophthalmology Virtual Education Library: NOVEL http://NOVEL.utah.edu |
| Publisher |
Spencer S. Eccles Health Sciences Library, University of Utah |
| Holding Institution |
North American Neuro-Ophthalmology Association. NANOS Executive Office 5841 Cedar Lake Road, Suite 204, Minneapolis, MN 55416 |
| Rights Management |
Copyright 2022. For further information regarding the rights to this collection, please visit: https://NOVEL.utah.edu/about/copyright |
| ARK |
ark:/87278/s6m8eg3m |
| Context URL |
The NANOS Annual Meeting Neuro-Ophthalmology Collection: https://novel.utah.edu/collection/NAM/toc/ |
| Contributor Primary |
Nancy J. Newman, MD |
| Contributor Secondary |
Patrick Yu-Wai-Man, Valerio Carelli, Prem Subramanyan4, Mark Moster, An-Guor Wang, Sean Donahue, Bart Leroy, Valérie Biousse, Catherine Vignal-Clermont, Alfredo Sadun, Gema Rebolleda Fernández, Elizabeth Fortin, Rudrani Banik, Laure Blouin, Michel Roux, Magali Taiel, José-Alain Sahe |
| Setname |
ehsl_novel_nam |
| ID |
2205270 |
| Reference URL |
https://collections.lib.utah.edu/ark:/87278/s6m8eg3m |
