| Identifier |
20150223_nanos_sciplatform1_02-1 |
| Title |
Preliminary Safety and Tolerability Results Of A Recombinant Adeno-Associated Viral Vector Serotype 2 (Raav2/2) Containing the Human Wild-Type Mitochondrial NADH Dehydrogenase 4 (ND4) Gene, in Patients with Leber Hereditary Optic Neuropathy Due to the G11778A Mitochondrial DNA Mutation |
| Creator |
Catherine Vignal, Graldine Honnet, Anne Galy, Nitza Thomasson, Marisol Corral Debrinsky, Scott Uretsky, Jean-Philippe Combal, Serge Fitoussi, Jose A. Sahel |
| Subject |
Leber Hereditary Optic Neuropathy, Mitochondrial Genetic Disorder, Gene Therapy, Adeno Associated Viral Vector, Safety and Tolerability Trial |
| Description |
Our goal is to report the results of a first-in-man safety trial of gene therapy in patients with Leber Hereditary Optic Neuropathy (LHON). |
| Date |
2015-02-23 |
| Language |
eng |
| Format |
application/pdf |
| Format Creation |
application/pdf |
| Type |
Text |
| Source |
2015 North American Neuro-Ophthalmology Society Annual Meeting |
| Relation is Part of |
NANOS Annual Meeting 2015 Platform Session 1 |
| Collection |
Neuro-ophthalmology Virtual Education Library: NOVEL http://NOVEL.utah.edu |
| Publisher |
Spencer S. Eccles Health Sciences Library, University of Utah |
| Holding Institution |
North American Neuro-Ophthalmology Association. NANOS Executive Office 5841 Cedar Lake Road, Suite 204, Minneapolis, MN 55416 |
| Rights Management |
Copyright 2013. For further information regarding the rights to this collection, please visit: https://NOVEL.utah.edu/about/copyright |
| ARK |
ark:/87278/s63n599n |
| Context URL |
The NANOS Annual Meeting Neuro-Ophthalmology Collection: https://novel.utah.edu/collection/NAM/toc/ |
| Contributor Primary |
Laura J. Balcer |
| Contributor Secondary |
Beau B. Bruce |
| Setname |
ehsl_novel_nam |
| ID |
185036 |
| Reference URL |
https://collections.lib.utah.edu/ark:/87278/s63n599n |
