Preliminary Safety and Tolerability Results Of A Recombinant Adeno-Associated Viral Vector Serotype 2 (Raav2/2) Containing the Human Wild-Type Mitochondrial NADH Dehydrogenase 4 (ND4) Gene, in Patients with Leber Hereditary Optic Neuropathy Due to the G11778A Mitochondrial DNA Mutation (Video)

Identifier	20150223_nanos_sciplatform1_02
Title	Preliminary Safety and Tolerability Results Of A Recombinant Adeno-Associated Viral Vector Serotype 2 (Raav2/2) Containing the Human Wild-Type Mitochondrial NADH Dehydrogenase 4 (ND4) Gene, in Patients with Leber Hereditary Optic Neuropathy Due to the G11778A Mitochondrial DNA Mutation (Video)
Creator	Catherine Vignal-Clermont; Geraldine Honnet; Anne Galy; Nitza Thomasson; Marisol Corral-Debrinsky; Scott Uretsky; Jean-Philippe Combal; Serge Fitoussi; Jose-Alain Sahel
Subject	Leber Hereditary Optic Neuropathy, Mitochondrial Genetic Disorder, Gene Therapy, Adeno Associated Viral Vector, Safety and Tolerability Trial
Description	Our goal is to report the results of a first-in-man safety trial of gene therapy in patients with Leber Hereditary Optic Neuropathy (LHON).
Date	2015-02-23
Language	eng
Format	video/mp4
Format Creation	application/video
Type	Image/MovingImage
Source	2015 North American Neuro-Ophthalmology Society Annual Meeting
Relation is Part of	NANOS Annual Meeting 2015 Scientific Platform Presentations (Session 1)
Collection	Neuro-ophthalmology Virtual Education Library: NOVEL http://NOVEL.utah.edu
Publisher	Spencer S. Eccles Health Sciences Library, University of Utah
Holding Institution	North American Neuro-Ophthalmology Association. NANOS Executive Office 5841 Cedar Lake Road, Suite 204, Minneapolis, MN 55416
Rights Management	Copyright 2015. For further information regarding the rights to this collection, please visit: https://NOVEL.utah.edu/about/copyright
ARK	ark:/87278/s64x8fmj
Context URL	The NANOS Annual Meeting Neuro-Ophthalmology Collection: https://novel.utah.edu/collection/NAM/toc/
Contributor Primary	Catherine Vignal-Clermont
Contributor Secondary	Geraldine Honnet; Anne Galy; Nitza Thomasson; Marisol Corral-Debrinsky; Scott Uretsky; Jean-Philippe Combal; Serge Fitoussi; Jose-Alain Sahel
Setname	ehsl_novel_nam
ID	184757
Reference URL	https://collections.lib.utah.edu/ark:/87278/s64x8fmj

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