Identifier |
20190319_nanos_posters_161 |
Title |
Long-term experience from an Expanded Access Program with idebenone in pediatric LHON patients |
Creator |
Xavier Llòria, Magda Silva, Claudia Catarino, Guenther Rudolph, Felice Lob, Bettina von Livonius, Thomas Klopstock |
Subject |
Optic Neuropathy |
Description |
LHON results in bilateral, severe central vision loss, and is caused by mitochondrial DNA mutations. LHON is typically diagnosed between 15 - 30 years of age, although it can be detected earlier. Idebenone, the only approved treatment for LHON in Europe, has been shown to be efficacious and safe in a large proportion of adult patients, but pediatric data is limited. The Expanded Access Program (EAP, a named patient program under local regulations) provides insights into the potential of idebenone in pediatric LHON. |
Date |
2019-03 |
Language |
eng |
Format |
application/pdf |
Source |
2019 North American Neuro-Ophthalmology Society Annual Meeting |
Relation is Part of |
NAM 2019: Poster Session II: Scientific Advancements in Neuro-Ophthalmology |
Collection |
Neuro-ophthalmology Virtual Education Library: NOVEL http://NOVEL.utah.edu |
Publisher |
Spencer S. Eccles Health Sciences Library, University of Utah |
Holding Institution |
North American Neuro-Ophthalmology Association. NANOS Executive Office 5841 Cedar Lake Road, Suite 204, Minneapolis, MN 55416 |
Rights Management |
Copyright 2019. For further information regarding the rights to this collection, please visit: https://NOVEL.utah.edu/about/copyright |
ARK |
ark:/87278/s6qr9fpc |
Context URL |
The NANOS Annual Meeting Neuro-Ophthalmology Collection: https://novel.utah.edu/collection/NAM/toc/ |
Contributor Primary |
Xavier Llòria |
Contributor Secondary |
Magda Silva, Claudia Catarino, Guenther Rudolph, Felice Lob, Bettina von Livonius, Thomas Klopstock |
Setname |
ehsl_novel_nam |
ID |
1432643 |
Reference URL |
https://collections.lib.utah.edu/ark:/87278/s6qr9fpc |