| Identifier |
20200310_nanos_sciplatform3_06-pdf |
| Title |
Expanded Access Program (EAP) in Leber's Hereditary Optic Neuropathy (LHON) Patients Treated for 24 Months (PDF) |
| Creator |
Thomas Klopstock; Xavier Llòria; Magda Silva; Rudolph Guenther; Felice Lob; Bettina Von Livonius; Claudia Catarino |
| Affiliation |
(TK) Friedrich-Baur-Institute, Dept. of Neurology University of Munich, MUNICH, Germany; (XL) (MS) Santhera Pharmaceuticals Ltd, Pratteln, Switzerland, Pratteln, Switzerland; (RG) (FL) (BV) (CC) Dep of Ophthalmology, University Hospital of the Ludwig-Maximilians University, Munich, Germany |
| Subject |
Optic Neuropathy |
| Description |
LHON is a mitochondrial genetic disorder resulting in severe bilateral central VA loss. Three primary mitochondrial DNA mutations cause over 90% of cases. Data from idebenone EAP for patients with LHON receiving treatment for at least 24 months were analyzed to assess rate of clinically-relevant recovery (CRR). |
| Date |
2020-03 |
| Language |
eng |
| Format |
application/pdf |
| Type |
Text |
| Source |
2020 North American Neuro-Ophthalmology Society Annual Meeting |
| Relation is Part of |
NANOS Annual Meeting 2020: Scientific Platform Session III |
| Collection |
Neuro-Ophthalmology Virtual Education Library: NANOS Annual Meeting Collection: https://novel.utah.edu/collection/nanos-annual-meeting-collection/ |
| Publisher |
North American Neuro-Ophthalmology Society |
| Holding Institution |
Spencer S. Eccles Health Sciences Library, University of Utah |
| Rights Management |
Copyright 2020. For further information regarding the rights to this collection, please visit: https://NOVEL.utah.edu/about/copyright |
| ARK |
ark:/87278/s66q76wd |
| Setname |
ehsl_novel_nam |
| ID |
1543306 |
| Reference URL |
https://collections.lib.utah.edu/ark:/87278/s66q76wd |
