Identifier |
20180306_nanos_posters_161 |
Title |
Baseline Characteristics of LHON Subjects in the RESCUE and REVERSE Phase III Gene Therapy Trials |
Creator |
Mark L. Moster; Catherine Vignal; Nancy Newman; Alfredo Sadun; Patrick Yu-Wai-Man; Valerio Carelli; Thomas Klopstock; Adam Debusk; Robert Sergott; Molly Scannel Bryan; Jose-Alain Sahel; Barrett Katz; Scott Uretsky |
Affiliation |
(MLM) Wills Eye Hospital and Sidney Kimmel Medical College of Thomas Jefferson University, Philadelphia, PA; (VC) Fondation A de Rothschild, Paris, France; (NN) Emory, Atlanta, GA; (AS) Doheny Eye Institute and UCLA, Los Angeles, CA; (PYWM) Wellcome Trust Centre and Moorfields Eye Hospital, London, United Kingdom; (VC) University of Bologna, Bologna, Italy; (TK) Friedrich-Baur-Institute, University Hospital of LMU, Munich, Germany; (AD) Wills Eye Hospital, Philadelphia, PA; (RS) Wills Eye Hospital and Optic Nerve Research Center, Philadelphia, PA; (MSB) University of Illinois, Chicago, IL; (JAS) Sorbonne Universites andUniversity of Pittsburgh, Paris and Pittsburgh, France; (BK) Albert Einstein College of Medicine, New York, NY; (SU) Gensight Biologics, Paris, France |
Subject |
Genetic Disease; Optic Neuropathy |
Description |
RESCUE and REVERSE are Phase‑ III, randomized, multicenter, double‑masked, sham‑ controlled trials of rAAV2/2-ND4, an intravitreally injected gene therapy for treatment of ND4‑ LHON. RESCUE subjects had vision loss for ≤6 months and REVERSE subjects from >6 months up to 1 year. |
Date |
2018-03 |
Language |
eng |
Format |
application/pdf |
Type |
Text |
Source |
2018 North American Neuro-Ophthalmology Society Annual Meeting |
Relation is Part of |
NANOS 2018: Poster Presentations |
Collection |
Neuro-ophthalmology Virtual Education Library: NOVEL http://NOVEL.utah.edu |
Publisher |
Spencer S. Eccles Health Sciences Library, University of Utah |
Holding Institution |
North American Neuro-Ophthalmology Association. NANOS Executive Office 5841 Cedar Lake Road, Suite 204, Minneapolis, MN 55416 |
Rights Management |
Copyright 2018. For further information regarding the rights to this collection, please visit: https://NOVEL.utah.edu/about/copyright |
ARK |
ark:/87278/s65q8w8p |
Context URL |
The NANOS Annual Meeting Neuro-Ophthalmology Collection: https://novel.utah.edu/collection/NAM/toc/ |
Setname |
ehsl_novel_nam |
ID |
1309581 |
Reference URL |
https://collections.lib.utah.edu/ark:/87278/s65q8w8p |