| Identifier |
20130212_nanos_sciplatform2_12-1 |
| Title |
Leber Hereditary Optic Neuropathy G11778A Gene Therapy Clinical Trial: Stability of Clinical Parameters in Preparatory Phase Based on Onset of Visual Loss |
| Creator |
Lam, Byron, L; Guy, John R: Feuer, William J; Porciatti, Vittorio; Vandenbroucke, Ruth; Schiffman, Joyce C |
| Subject |
Leber Hereditary Optic neuropathy; Gene Therapy |
| Description |
The preparatory phase of the LHON gene therapy trial aims to characterize affected patients and carriers for the planned gene therapy study that will utilize "allotopic expression" via an adeno-associated virus vector. We have followed the natural history of affected patients to characterize visual function outcome variables for the planned phase I and II studies. |
| Date |
2013-02-12 |
| Language |
eng |
| Format |
application/pdf |
| Format Creation |
application/PowerPoint |
| Type |
Text |
| Source |
2013 North American Neuro-Ophthalmology Society Annual Meeting |
| Relation is Part of |
NANOS 2013: Platform Presentations (Session II) |
| Collection |
Neuro-ophthalmology Virtual Education Library: NOVEL http://NOVEL.utah.edu |
| Publisher |
Spencer S. Eccles Health Sciences Library, University of Utah |
| Holding Institution |
North American Neuro-Ophthalmology Association. NANOS Executive Office 5841 Cedar Lake Road, Suite 204, Minneapolis, MN 55416 |
| Rights Management |
Copyright 2013. For further information regarding the rights to this collection, please visit: https://NOVEL.utah.edu/about/copyright |
| ARK |
ark:/87278/s6r2472b |
| Context URL |
The NANOS Annual Meeting Neuro-Ophthalmology Collection: https://novel.utah.edu/collection/NAM/toc/ |
| Contributor Primary |
Bose, Suwaraj |
| Contributor Secondary |
McCulley, Timothy J |
| Setname |
ehsl_novel_nam |
| ID |
183336 |
| Reference URL |
https://collections.lib.utah.edu/ark:/87278/s6r2472b |
