Identifier |
20200312_nanos_newtreatmentsno1_05-pdf |
Title |
Gene Therapy - Evolution and Therapeutic Applications (PDF) |
Creator |
Patrick Yu-Wai-Man |
Affiliation |
University of Cambridge and Moorfields Eye Hospital, United Kingdom |
Subject |
Gene Therapy; Genome Editing; Mitochondrial Diseases; Neurodegenerative Diseases; Viral Vectors |
Description |
Gene therapy is an attractive treatment strategy for both inherited and acquired late-onset neurodegenerative diseases (1). Over the past three decades, significant advances have been made in gene delivery methods and achieving more targeted and sustained expression of the gene of interest. The promising results obtained from preclinical studies have led to an increasing number of human clinical trials to investigate the safety and efficacy of gene therapy approaches for a broad range of disorders, in particular those involving the eye and the central nervous system. |
Date |
2020-03 |
Language |
eng |
Format |
application/pdf |
Type |
Text |
Source |
2020 North American Neuro-Ophthalmology Society Annual Meeting |
Relation is Part of |
NANOS Annual Meeting 2020: New Treatments in Neuro-Ophthalmology-2020 Trends |
Collection |
Neuro-ophthalmology Virtual Education Library: NOVEL http://NOVEL.utah.edu |
Publisher |
Spencer S. Eccles Health Sciences Library, University of Utah |
Holding Institution |
North American Neuro-Ophthalmology Association. NANOS Executive Office 5841 Cedar Lake Road, Suite 204, Minneapolis, MN 55416 |
Rights Management |
Copyright 2020. For further information regarding the rights to this collection, please visit: https://NOVEL.utah.edu/about/copyright |
ARK |
ark:/87278/s6ms93gz |
Context URL |
The NANOS Annual Meeting Neuro-Ophthalmology Collection: https://novel.utah.edu/collection/NAM/toc/ |
Setname |
ehsl_novel_nam |
ID |
1543343 |
Reference URL |
https://collections.lib.utah.edu/ark:/87278/s6ms93gz |