| Identifier |
20130212_nanos_sciplatform2_12 |
| Title |
Leber Hereditary Optic Neuropathy G11778A Gene Therapy Clinical Trial: Stability of Clinical Parameters in Preparatory Phase Based on Onset of Visual Loss |
| Creator |
Byron L. Lam; John R. Guy; William J. Feuer; Vittorio Porciatti; Ruth Vandenbroucke; Joyce C. Schiffman |
| Affiliation |
(BLL) Bascom Palmer Eye Institute, University of Miami, Miami, FL |
| Subject |
Leber Hereditary Optic Neuropathy; Gene Therapy |
| Description |
The preparatory phase of the LHON gene therapy trial aims to characterize affected patients and carriers for the planned gene therapy study that will utilize 'allotopic expression' via an adeno-associated virus vector. We have followed the natural history of affected patients to characterize visual function outcome variables for the planned phase I and II studies. |
| Date |
2013-02-12 |
| Language |
eng |
| Format |
application/pdf |
| Type |
Text |
| Source |
2013 North American Neuro-Ophthalmology Society Annual Meeting |
| Relation is Part of |
NANOS 2013: Platform Presentations (Session II) |
| Collection |
Neuro-Ophthalmology Virtual Education Library: NANOS Annual Meeting Collection: https://novel.utah.edu/collection/nanos-annual-meeting-collection/ |
| Publisher |
North American Neuro-Ophthalmology Society |
| Holding Institution |
Spencer S. Eccles Health Sciences Library, University of Utah |
| Rights Management |
Copyright 2013. For further information regarding the rights to this collection, please visit: https://NOVEL.utah.edu/about/copyright |
| ARK |
ark:/87278/s6962q7z |
| Setname |
ehsl_novel_nam |
| ID |
183293 |
| Reference URL |
https://collections.lib.utah.edu/ark:/87278/s6962q7z |
