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Title | Creator | Description | Identifier |
1 |
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Leber Hereditary Optic Neuropathy G11778A Gene Therapy Clinical Trial: Stability of Clinical Parameters in Preparatory Phase Based on Onset of Visual Loss | Lam, Byron, L; Guy, John R: Feuer, William J; Porciatti, Vittorio; Vandenbroucke, Ruth; Schiffman, Joyce C | The preparatory phase of the LHON gene therapy trial aims to characterize affected patients and carriers for the planned gene therapy study that will utilize "allotopic expression" via an adeno-associated virus vector. We have followed the natural history of affected patients to characterize visual ... | 20130212_nanos_sciplatform2_12 |
2 |
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Leber Hereditary Optic Neuropathy G11778A Gene Therapy Clinical Trial: Stability of Clinical Parameters in Preparatory Phase Based on Onset of Visual Loss | Lam, Byron, L; Guy, John R: Feuer, William J; Porciatti, Vittorio; Vandenbroucke, Ruth; Schiffman, Joyce C | The preparatory phase of the LHON gene therapy trial aims to characterize affected patients and carriers for the planned gene therapy study that will utilize "allotopic expression" via an adeno-associated virus vector. We have followed the natural history of affected patients to characterize visual ... | 20130212_nanos_sciplatform2_12-1 |