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1 Leber Hereditary Optic Neuropathy G11778A Gene Therapy Clinical Trial: Stability of Clinical Parameters in Preparatory Phase Based on Onset of Visual LossLam, Byron, L; Guy, John R: Feuer, William J; Porciatti, Vittorio; Vandenbroucke, Ruth; Schiffman, Joyce CThe preparatory phase of the LHON gene therapy trial aims to characterize affected patients and carriers for the planned gene therapy study that will utilize "allotopic expression" via an adeno-associated virus vector. We have followed the natural history of affected patients to characterize visual ...20130212_nanos_sciplatform2_12
2 Leber Hereditary Optic Neuropathy G11778A Gene Therapy Clinical Trial: Stability of Clinical Parameters in Preparatory Phase Based on Onset of Visual LossLam, Byron, L; Guy, John R: Feuer, William J; Porciatti, Vittorio; Vandenbroucke, Ruth; Schiffman, Joyce CThe preparatory phase of the LHON gene therapy trial aims to characterize affected patients and carriers for the planned gene therapy study that will utilize "allotopic expression" via an adeno-associated virus vector. We have followed the natural history of affected patients to characterize visual ...20130212_nanos_sciplatform2_12-1
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