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Long Term Treatment with Idebenone in Leber's Hereditary Optic Neuropathy (LHON): Real World Clinical Practice | Xavier Llòria, Claudia Catarino, Magda Silva, Bettina von Livonius, Constanze Gallenmüller, Felice Lob, Günther Rudolph, Oskars Mikazans, Thomas Klopstock | LHON is caused by mitochondrial DNA (mtDNA) mutations, resulting in progressive bilateral, severe central blindness. Idebenone (900 mg/day) is approved for use in LHON in the EU . We report long-term treatment outcomes in real-world clinical practice from a multicenter Expanded Access Program. | 20180306_nanos_posters_152 |