| Identifier |
20160301_nanos_sciplatform2_09 |
| Title |
Recombinant AAV2 Containing the Wild-Type ND4 Gene (rAAV2/2-ND4) is an Experimental Gene Therapy for Vision Loss in LHON Due to the ND4 Mitochondrial Mutation: Phase I/IIa Safety Investigation Results and Upcoming Pivotal Phase III Efficacy Studies (.pdf) |
| Creator |
Catherine Vignal |
| Subject |
Optic Neuropathy, Genetic Disease |
| Description |
Allotopic expression of the wild-type ND4 gene delivered by a rAAV2/2 vector through intra-vitreal injection is an experimental therapy for vision loss in patients with ND4 LHON. |
| Date |
2016-03-01 |
| Language |
eng |
| Format |
application/pdf |
| Format Creation |
application/pdf |
| Type |
Text |
| Relation is Part of |
NANOS Annual Meeting 2016: Scientific Platform Session II |
| Collection |
Neuro-ophthalmology Virtual Education Library: NOVEL http://NOVEL.utah.edu |
| Publisher |
Spencer S. Eccles Health Sciences Library, University of Utah |
| Holding Institution |
North American Neuro-Ophthalmology Association. NANOS Executive Office 5841 Cedar Lake Road, Suite 204, Minneapolis, MN 55416 |
| ARK |
ark:/87278/s67t0vnt |
| Context URL |
The NANOS Annual Meeting Neuro-Ophthalmology Collection: https://novel.utah.edu/collection/NAM/toc/ |
| Contributor Primary |
Catherine Vignal, Scott Uretsky, Nitza Thomasson, Geraldine Honnet, Marisol Corral-Debrinski, Celine Bouquet, Anne Galy, Jean-Philippe Combal, Serge Fitoussi, José A. Sahel |
| Setname |
ehsl_novel_nam |
| ID |
185329 |
| Reference URL |
https://collections.lib.utah.edu/ark:/87278/s67t0vnt |
