| Identifier |
20170404_nanos_sciplatform2_09 |
| Title |
Phase I/IIa Visual Acuity Outcomes 1.5-Years Post-Treatment with rAAV2/2-ND4,; Investigational Gene Therapy for ND4 LHON (video) |
| Creator |
Catherine Vignal, Scott Uretsky, Nitza Thomasson, Céline Bouquet, Anne Galy, Jean Philippe Combal, Serge Fitoussi, Jose Aalin Sahel |
| Subject |
Genetic Disease; Optic Neuropathy |
| Description |
rAAV2/2-ND4 is an experimental gene therapy enabling allotopic transgene expression. We report visual acuity (VA) outcomes 1.5- years post-treatment in a Phase I/IIa (NCT02064569) open-label, dose-escalation safety study. |
| Date |
2017-04-04 |
| Language |
eng |
| Format |
video/mp4 |
| Source |
2017 North American Neuro-Ophthalmology Society Annual Meeting |
| Relation is Part of |
NANOS Annual Meeting 2017: Scientific Platform Presentations (Session 2) |
| Collection |
Neuro-ophthalmology Virtual Education Library: NOVEL http://NOVEL.utah.edu |
| Publisher |
Spencer S. Eccles Health Sciences Library, University of Utah |
| Holding Institution |
North American Neuro-Ophthalmology Association. NANOS Executive Office 5841 Cedar Lake Road, Suite 204, Minneapolis, MN 55416 |
| Rights Management |
Copyright 2017. For further information regarding the rights to this collection, please visit: https://NOVEL.utah.edu/about/copyright |
| ARK |
ark:/87278/s60p4tj1 |
| Context URL |
The NANOS Annual Meeting Neuro-Ophthalmology Collection: https://novel.utah.edu/collection/NAM/toc/ |
| Contributor Primary |
Catherine Vignal |
| Contributor Secondary |
Scott Uretsky, Nitza Thomasson, Céline Bouquet, Anne Galy, Jean Philippe Combal, Serge Fitoussi, Jose Aalin Sahel |
| Setname |
ehsl_novel_nam |
| ID |
1276731 |
| Reference URL |
https://collections.lib.utah.edu/ark:/87278/s60p4tj1 |
